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MedicineChemistry

Selective silencing of expanded CAG repeats: Chemically modified siRNA advances RNA-based therapies for polyglutamine diseases.

Gijs-Jan Scholten, Jim Hyde, Ronald A. M. Buijsen

2026.3.1Molecular Therapy Nucleic Acids

DOI: 10.1016/j.omtn.2026.102869

Abstract

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Citation format

SCHOLTEN, Gijs-Jan; HYDE, Jim; BUIJSEN, Ronald A. M. Selective silencing of expanded CAG repeats: Chemically modified sirna advances RNA-based therapies for polyglutamine diseases. Molecular Therapy Nucleic Acids, 2026, 37 1(1): 102869.