Spk-8011: Preliminary Results from a Phase 1/2 Dose Escalation Trial of an Investigational AAV-Mediated Gene Therapy for Hemophi | AcademicGPT, tlooto

The study is evaluating the safety, tolerability and efficacy of a single intravenous infusion of SPK-8011 in up to 18 adult men with hemophilia A, a recombinant AAV vector composed of a bio-engineere (2017), BLOOD, George Lindsey A. | AcademicGPT, tlooto for Academic and Research